Found 6 matching trials
A Global Prospective Observational Registry of Patients With Pompe Disease
N/AThis is a global, multicenter, prospective, observational registry of patie...
Location
University of Arkansas Medical Science
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
PHASE3This is a Phase 3, open-label, multicenter study to evaluate the safety, ef...
Location
University of Florida Clinical Research Center
First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221
PHASE1This is an international, multi-center, open-label study designed to evalua...
Location
Neuromuscular Research Centre
A Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe Disease
PHASE3This is a phase 3 double-blind randomized study to study the efficacy and s...
Location
Neuromuscular Research Center
A Study to Assess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD)
PHASE3This is a multicenter, international open-label extension study of ATB200/A...
Location
University of Arkansas for Medical Sciences
ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD
PHASE3This is a Phase 3, open-label, multicenter study to evaluate the safety, PK...
Status
Active Not Recruiting
Location
University of Florida Clinical Research Center